The effect of human gene therapy for RPE65 -associated Leber’s congenital amaurosis on visual function: a systematic review and meta-analysis | Orphanet Journal of Rare Diseases | Full Text

The effect of human gene therapy for RPE65 -associated Leber’s congenital amaurosis on visual function: a systematic review and meta-analysis | Orphanet Journal of Rare Diseases | Full Text

The effect of human gene therapy for RPE65-associated Leber’s congenital amaurosis on visual function: a systematic review and meta-analysis

RPE65-associated LCA (RPE65-LCA) is an inherited retinal degeneration caused by the mutations of RPE65 gene and gene therapy has been developed to be a promising treatment. This study aims to evaluate the associa...

Authors:Xue Wang, Chaofeng Yu, Radouil T. Tzekov, Yihua Zhu and Wensheng Li

Citation:Orphanet Journal of Rare Diseases 2020 15:49

Content type:Review

Published on: 14 February 2020

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