Orphanet Journal of Rare Diseases | Home page

Orphanet Journal of Rare Diseases | Home page

Orphanet Journal of Rare Diseases

The following new articles have just been published in Orphanet Journal of Rare Diseases RESEARCH Development and validation of the prognostic value of ferritin in adult patients with Hemophagocytic Lymphohistiocytosis Jun Zhou, Jing Zhou, Dan-Ting Shen, Hemant Goyal, Zhi-Qi Wu and Hua-Guo Xu Orphanet Journal of Rare Diseases 2020, 15:71 | Published on: 12 March 2020 Full Text | PDF REVIEW A roadmap to using historical controls in clinical trials – by Drug Information Association Adaptive Design Scientific Working Group (DIA-ADSWG) Mercedeh Ghadessi, Rui Tang, Joey Zhou, Rong Liu, Chenkun Wang, Kiichiro Toyoizumi, Chaoqun Mei, Lixia Zhang, C. Q. Deng and Robert A. Beckman Orphanet Journal of Rare Diseases 2020, 15:69 | Published on: 12 March 2020 Full Text | PDF REVIEW Health, wellbeing and lived experiences of adults with SMA: a scoping systematic review Hamish W. Y. Wan, Kate A. Carey, Arlene D’Silva, Steve Vucic, Matthew C. Kiernan, Nadine A. Kasparian and Michelle A. Farrar Orphanet Journal of Rare Diseases 2020, 15:70 | Published on: 12 March 2020 Full Text | PDF

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