To what degree are orphan drugs patient-centered? A review of the current state of clinical research in rare diseases | Orphanet Journal of Rare Diseases | Full Text

To what degree are orphan drugs patient-centered? A review of the current state of clinical research in rare diseases | Orphanet Journal of Rare Diseases | Full Text

1. To what degree are orphan drugs patient-centered? A review of the current state of clinical research in rare diseases

   Over the past 30 years, the healthcare industry has increasingly turned its attention to rare diseases. Regulators have emphasized the need for clinical research in this area to be patient-centered. However, t...

   Authors:Sally Lanar, Catherine Acquadro, James Seaton, Isabelle Savre and Benoit Arnould

   Citation:Orphanet Journal of Rare Diseases 2020 15:134

   Content type:Review

    

   Published on: 3 June 2020

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