Una terapia basada en ARN de transferencia restaura la función génica en modelos de fibrosis quística.

Nonviral delivery of chemically modified tRNA rescues nonsense mutations in cystic fibrosis Jingan Chen https://orcid.org/0009-0002-5105-102X, Muye Zhou https://orcid.org/0009-0008-8827-0609, Songtao Dong https://orcid.org/0009-0000-6841-6924, Fanglin Gong https://orcid.org/0009-0003-4776-9351, Rasangi Tennakoon, Breanna Y. Seto https://orcid.org/0009-0006-6888-1811, Ziyan Rachel Chen, Zhichang Peter Zhou https://orcid.org/0000-0001-9548-9491, Jingyi Pan, [...] , and Bowen Li https://orcid.org/0000-0001-5006-9143 https://www.science.org/doi/10.1126/science.aeb0054?utm_medium=email&_hsenc=p2ANqtz-8WNj7OrD1P7-aZ_b7DCef3lE_ftvN6ax4tSvPJ8xo06dgmm1RWaQ-akQmjyAMO94C6_IXLmoCBrNMmtorObIAJwLcRsw&_hsmi=144840094&utm_content=144848639&utm_source=hs_email