Cystic Fibrosis News Today Daily Digest

Cystic Fibrosis Weekly Update Contents: Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29 We Need to Change Our Language When Discussing Mental Health FDA Grants Fast Track Status to Translate Bio’s RNA-Based Therapy MRT5005 My Experience with Trikafta Has Been More Difficult Than Expected Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29 Mar 02, 2020 10:34 am | Mary Chapman Beginning on Feb. 29, Rare Disease Day, chapters from notable scientific books and clinical review articles covering rare disorders will be available free-of-charge from Elsevier. The offer runs through April 30, and aims to supports work by researchers and clinicians into a better understanding of and treatments for rare diseases, as well as to raise awareness about these ills. […] The post Elsevier Opens Books, Review Articles to Rare Disease Researchers Starting Feb. 29 appeared first on Cystic Fibrosis News Today. Read More We Need to Change Our Language When Discussing Mental Health Mar 02, 2020 09:00 am | Tré LaRosa My brain felt broken. I didn’t know what to do, even after three years of dealing with depression and anxiety. Our language around our mental health discourse is woefully insufficient. We don’t treat depression or anxiety the way we treat diabetes or cystic fibrosis or heart disease. We treat it like a sprained ankle. While […] The post We Need to Change Our Language When Discussing Mental Health appeared first on Cystic Fibrosis News Today. Read More FDA Grants Fast Track Status to Translate Bio’s RNA-Based Therapy MRT5005 Mar 02, 2020 07:00 am | Marisa Wexler MS The U.S. Food and Drug Administration (FDA) has granted fast track designation to MRT5005, an investigational RNA-based treatment for cystic fibrosis (CF), the therapy’s developer, Translate Bio, has announced. Fast track is given to medications that aim to treat serious or life-threatening conditions and that have the potential to fill unmet medical needs to expedite […] The post FDA Grants Fast Track Status to Translate Bio’s RNA-Based Therapy MRT5005 appeared first on Cystic Fibrosis News Today. Read More My Experience with Trikafta Has Been More Difficult Than Expected Feb 28, 2020 03:00 pm | Elizabeth Rogers I’ve been fortunate to start taking Trikafta, a next-generation, triple-combination treatment for cystic fibrosis. My journey began in December, but it hasn’t been the easiest path to walk along, as I’ve encountered unexpected twists and turns. How Trikafta affects someone’s relationship with their body varies from person to person. But I feel as though I’ve […] The post My Experience with Trikafta Has Been More Difficult Than Expected appeared first on Cystic Fibrosis News Today. Read More   Recent News Organoid-Based Personalized Medicine Trial Enrollment Complete CFTR Amplifiers May Be Potent CF Mono or Combo Therapy, Study Says Advice on Starting Nonprofit Groups for Rare and Other Diseases Focus of NORD Webinar UK NICE to Announce Decision on Vertex’s Therapy Trikafta in December Being Sick Doesn’t Give Me a Free Pass to Be Disrespectful