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Last Posted: Jul 10, 2020
- Latin American consensus on the supportive management of patients with severe combined immunodeficiency.
Bustamante Ogando Juan Carlos et al. The Journal of allergy and clinical immunology 2019 144(4) 897-905 - What does the 'Cochrane database of systematic reviews' tell us about hemophilia?
Rodriguez-Merchan Emerito-Carlos et al. Expert review of hematology 2019 12(11) 919-922 - Clearing the path for gene therapy
B Gyorgy, Sci Trans Med, July 8, 2020 - Patient and family social media use surrounding a novel treatment for a rare genetic disease: a qualitative interview study.
Iyer Alexander A et al. Genetics in medicine : official journal of the American College of Medical Genetics 2020 Jun - FDA orphan drug designations for lysosomal storage disorders - a cross-sectional analysis.
Garbade Sven F et al. PloS one 2020 15(4) e0230898 - Gene and Stem Cell Therapies for Fetal Care- A Review
AE O'Connell, JAMA Pediatrics, June 29, 2020 - A ‘Cure for Heart Disease’? A Single Shot Succeeds in Monkeys A novel gene-editing experiment seems to have permanently reduced LDL and triglyceride levels in monkeys.
G Kolata, NY Times, June 2020 - Here's how genes from Covid-19 survivors could help you--Gene therapy could put an end to future pandemics.
Regalado A. MIT Tech Review, Jun 18, 2020. - Here’s how genes from covid-19 survivors could help you- Gene therapy could put an end to future pandemics.
A Regalado, MIT Tech Review, June 18, 2020 - Advances in Sickle Cell Disease Treatments.
Pavan Aline Renata et al. Current medicinal chemistry 2020 Jun
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