Positive association between physical outcomes and patient-reported outcomes in late-onset Pompe disease: a cross sectional study | Orphanet Journal of Rare Diseases | Full Text

Positive association between physical outcomes and patient-reported outcomes in late-onset Pompe disease: a cross sectional study | Orphanet Journal of Rare Diseases | Full Text

Positive association between physical outcomes and patient-reported outcomes in late-onset Pompe disease: a cross sectional study

Pompe disease is a rare, progressive metabolic myopathy. The aim of this study is to investigate the associations of physical outcomes with patient-reported outcome measures (PROMs) in late-onset Pompe disease.

Authors:Meng Yuan, Eleni-Rosalina Andrinopoulou, Michelle E. Kruijshaar, Aglina Lika, Laurike Harlaar, Ans T. van der Ploeg, Dimitris Rizopoulos and Nadine A. M. E. van der Beek

Citation:Orphanet Journal of Rare Diseases 2020 15:232

Content type:Research

 

Published on: 3 September 2020

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