Registries for orphan drugs: generating evidence or marketing tools? | Orphanet Journal of Rare Diseases | Full Text

Registries for orphan drugs: generating evidence or marketing tools? | Orphanet Journal of Rare Diseases | Full Text

Registries for orphan drugs: generating evidence or marketing tools?

Independent disease registries for pre-and post-approval of novel treatments for rare diseases are increasingly important for healthcare professionals, patients, regulators and the pharmaceutical industry. Cur...

Authors:Carla E. M. Hollak, Sandra Sirrs, Sibren van den Berg, Vincent van der Wel, Mirjam Langeveld, Hanka Dekker, Robin Lachmann and Saco J. de Visser

Citation:Orphanet Journal of Rare Diseases 2020 15:235

Content type:Position statement

 

Published on: 3 September 2020

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