Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease | Orphanet Journal of Rare Diseases | Full Text

Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease | Orphanet Journal of Rare Diseases | Full Text

Patient reported outcome measures in a large cohort of patients with type 1 Gaucher disease

It is now acknowledged that the input of patients in health outcome assessment is vital to understanding the impact of diseases and interventions for those diseases. This study is the first report of patient-r...

Authors:Tama Dinur, Majdolen Istaiti, Dafna Frydman, Michal Becker-Cohen, Jeff Szer, Ari Zimran and Shoshana Revel-Vilk

Citation:Orphanet Journal of Rare Diseases 2020 15:284

Content type:Research

 

Published on: 13 October 2020

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