Cystic Fibrosis Weekly Update

Contents:

Symdeko and Orkambi Seen to Also Ease Inflammation in CF Patients

May 22, 2020 07:00 am | Ines Martins, PhD

In addition to restoring CFTR protein function in cells, the cystic fibrosis (CF) therapies Orkambi (lumacaftor/ivacaftor) and Symdeko (tezacaftor/ivacaftor combo) significantly reduce the excessive inflammation that damages patients’ lungs, a recent study suggests. Symdeko seems to be more potent than Orkambi at dampening inflammatory responses. The study, “Different CFTR modulator combinations downregulate inflammation differently in cystic […]
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Young CF Patients in UK Receive Machines for At-home Lung Monitoring During Pandemic

May 21, 2020 07:00 am | Ines Martins, PhD

Oxford Hospitals Charity has purchased and delivered machines able to measure lung function at home to 120 young patients with cystic fibrosis (CF) in the U.K., enabling them to closely monitor their condition during the COVID-19 pandemic. The mini lung function machines were funded with the help of NHS Charities Together, and sent to patients […]
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Unity and EU-wide Efforts Focus of Online Rare Disease Meeting

May 20, 2020 09:30 am | Larry Luxner

Eurordis, a Paris-based coalition of national rare disease associations across Europe, hosted its first all-virtual conference, bringing some 1,500 delegates from 57 countries together online during the COVID-19 pandemic. The 10th European Conference on Rare Diseases & Orphan Products (ECRD2020) — which was set for May 14–15 in Stockholm, instead took place via Zoom. Eurordis […]
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