Cystic Fibrosis Weekly Update

Contents:

Proteostasis to Test Personalized Treatment with Novel CFTR Modulators in Europe

Dec 13, 2019 07:00 am | Ana Pena, PhD

Three investigative therapies by Proteostasis Therapeutics — PTI-801, PTI-808, and PTI-428 — showed potential to treat cystic fibrosis (CF) patients ineligible for approved CFTR modulators after patient-specific lab models produced promising results that support a future clinical trial. Funded by the EU’s initiative HIT-CF (Human Individualized Therapy of CF), this early study was conducted on […]
The post Proteostasis to Test Personalized Treatment with Novel CFTR Modulators in Europe appeared first on Cystic Fibrosis News Today.

I’m Sharing My Friend’s Story with Hope of a Triple-organ Transplant

Dec 12, 2019 03:00 pm | Luisa Palazola

In this column, I want to share the story of a friend who needs a triple-organ transplant: lungs, liver, and kidneys. Before I delve into his experience, I’d like to provide some context about me. I have cystic fibrosis (CF), and through my writing, I was offered a position as Community Manager at Cystic Fibrosis […]
The post I’m Sharing My Friend’s Story with Hope of a Triple-organ Transplant appeared first on Cystic Fibrosis News Today.

CFF Offers Emotional Send-off to Retiring CEO Preston Campbell

Dec 12, 2019 07:00 am | Larry Luxner

Preston W. Campbell III, MD, recently bid farewell as president and CEO of the Cystic Fibrosis Foundation (CFF) in Nashville — the same city where he began his long association with the disease 30 years ago as a pediatric pulmonologist at Vanderbilt University’s Cystic Fibrosis (CF) Care Center. Campbell’s last day at CFF is Dec. […]
The post CFF Offers Emotional Send-off to Retiring CEO Preston Campbell appeared first on Cystic Fibrosis News Today.