Gene therapy [NEW TOPIC PAGE]

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From National Institutes of Health Web Sites

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• Gene Therapy for Eye Disease Shows Benefits and Limitations Gene Therapy for Eye Disease Shows Benefits and Limitations  
  NIH Research Matters, May 18, 2015
• Gene therapy shows promise for treating Niemann-Pick disease type C1  
  NIH, October 26, 2016
• Snapshots of Life: Lighting up the Promise of Retinal Gene Therapy  
  Francis Collins, NIH Director, November 10, 2016