Cystic Fibrosis News Today Weekly Digest

Cystic Fibrosis Weekly Update Contents: French Authorities Approve Reimbursement of Orkambi for CF Patients 2 Years and Older NIH Grants $2.7M for Research on Anaerobic Bacteria’s Role in CF Flare-ups Attending This Year’s North American Cystic Fibrosis Conference Gave Me Hope French Authorities Approve Reimbursement of Orkambi for CF Patients 2 Years and Older Nov 22, 2019 07:00 am | Iqra Mumal MSc The Comité Économique des Produits de Santé (CEPS) in France has approved national reimbursement of Vertex Pharmaceuticals’ Orkambi (lumacaftor/ivacaftor) for patients with cystic fibrosis (CF) who are 2 years of age or older, with two copies of the F508del mutation in the cystic fibrosis transmembrane conductance regulator (CFTR) gene (the gene defective in CF). Once the agreement has […] The post French Authorities Approve Reimbursement of Orkambi for CF Patients 2 Years and Older appeared first on Cystic Fibrosis News Today. Read More NIH Grants $2.7M for Research on Anaerobic Bacteria’s Role in CF Flare-ups Nov 21, 2019 07:00 am | Iqra Mumal MSc The National Institutes of Health (NIH) has granted $2.7 million to Michigan State University (MSU) scientist Robert Quinn to investigate, in collaboration with Spectrum Health, the role of anaerobic bacteria in the development of flare-ups among patients with cystic fibrosis (CF). Anaerobic bacteria are a type of bacteria that live without oxygen, and are frequently […] The post NIH Grants $2.7M for Research on Anaerobic Bacteria’s Role in CF Flare-ups appeared first on Cystic Fibrosis News Today. Read More Attending This Year’s North American Cystic Fibrosis Conference Gave Me Hope Nov 20, 2019 03:00 pm | Ella Balasa Two weeks ago, I watched a livestream of the North American Cystic Fibrosis Conference (NACFC) as I popped Trikafta (elexacaftor/tezacaftor/ivacaftor) tablets out of their blister pack. Francis Collins, one of the researchers who discovered the cystic fibrosis transmembrane conductance regulator (CFTR) gene, was singing to an audience of thousands. I teared up when he sang, “Dare […] The post Attending This Year’s North American Cystic Fibrosis Conference Gave Me Hope appeared first on Cystic Fibrosis News Today. Read More Recent News CF-related Diabetes Affects Girls More Often and at Younger Age than Boys, European Study Shows A Rare Disease Film Festival Made Me Ponder Our Future Fight for Others UI Researchers Develop Breakthrough Approach to Gene Therapies for Respiratory Diseases Starting Trikafta with Hope for the CF Community Discovered Bacteria ‘Wars’ May Lead to New Antimicrobial Treatments for CF, Study Suggests