Cystic Fibrosis News Today Weekly Digest

Cystic Fibrosis Weekly Update Contents: Positive Data from VX-445 Triple Combo Regimen Prompt Vertex to Seek Regulatory Approval Window for More Effective Treatment of CF Lung Infections is 2 to 3 Years, Study Suggests How Does Cystic Fibrosis Affect Our Fear of Failure? NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research Positive Data from VX-445 Triple Combo Regimen Prompt Vertex to Seek Regulatory Approval Mar 08, 2019 07:00 am | Alice Melão Vertex Pharmaceuticals is planning to request regulatory approval from the U.S. Food and Drug Administration (FDA) and the European Medicines Agency (EMA) during the third and fourth quarters of 2019, respectively, for VX-659 or VX-445 triple combination regimens. If approved, these new combo therapies will represent an alternative and effective strategy to treat cystic fibrosis (CF) […] The post Positive Data from VX-445 Triple Combo Regimen Prompt Vertex to Seek Regulatory Approval appeared first on Cystic Fibrosis News Today. Read More Window for More Effective Treatment of CF Lung Infections is 2 to 3 Years, Study Suggests Mar 07, 2019 11:30 am | Jose Marques Lopes, PhD Treatment of Pseudomonas aeruginosa lung infections in cystic fibrosis (CF) patients could be more effective if done within a crucial two- to three-year period when the bacteria are still susceptible to antibiotics, according to a study. The study, “Evolutionary highways to persistent bacterial infection,” was published in the journal Nature Communications. Genetic changes that have accumulated over […] The post Window for More Effective Treatment of CF Lung Infections is 2 to 3 Years, Study Suggests appeared first on Cystic Fibrosis News Today. Read More How Does Cystic Fibrosis Affect Our Fear of Failure? Mar 07, 2019 09:00 am | Elly Aylwin-Foster I was made redundant last year. A week later, I turned 30. One week after that, I found out that I had failed to make it into the preliminary stages of the first publishing competition I’d entered. Then the following week, I was admitted to hospital with one hell of a cystic fibrosis (CF) exacerbation. […] The post How Does Cystic Fibrosis Affect Our Fear of Failure? appeared first on Cystic Fibrosis News Today. Read More NIH Rare Disease Day Highlights Joint Networks Advancing Array of Research Mar 07, 2019 07:00 am | Susan Boswell Rare diseases affect about 30 million Americans — roughly the same number as those with type 2 diabetes. Yet only 5 percent of the estimated 7,000 rare diseases known to science have cures or treatments approved by the U.S. Food and Drug Administration (FDA). Raising awareness of those illnesses and highlighting the promise of new therapies […] The post NIH Rare Disease Day Highlights Joint Networks Advancing Array of Researchappeared first on Cystic Fibrosis News Today. Read More   Recent News Translate Bio Advancing MRT5005 Through Ongoing Phase 1/2 Trial in CF Patients MaRS Innovation Supports LAB150 Research on New Therapeutics for CF and Other Conditions Don’t Distance Yourself from Your OG Carers The Power of Escapism European HIT-CF Project to Explore ELX-02 as Treatment for Rare CF Mutations