MESA REDONDA DE COMPAÑÍAS DE EURORDIS
The Voice of Rare Disease
Patients in Europe
24th Workshop of the EURORDIS Round Table of Companies: "Bringing solutions to young rare disease patients"
24th Workshop of the EURORDIS Round Table of Companies
"Bringing solutions to young rare disease patients"
Let's discuss the paediatric regulation
- Increased training and engagement of parents and young patients (conditions of success and type of training needed)
- How Extrapolation and design of Small Population Clinical Trials (SPCTs) can help
- How to make PIP work for rare diseases? What can industry do to perform more studies on children?
Universitat Autònoma de Barcelona
C/Sant Antoni Maria Claret, 171 (corner of Sant Quinti)